Meet the Global Team Working to Understand and Advance Treatments for NF1

The executive team that determines strategic priorities and directs our work.

The experts across neurology, dermatology, oncology, biotech, higher ed, engineering, and gene therapy who advise our work.

The team that brings our mission to life.

Executive Leadership

First Last Name,
M.D., Ph.D., Chair
Title

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Advisors

Dr. Federico Mingozzi
Ph.D.
Gene Therapy Acceleration Committee
Dr. Lu Le
M.D., Ph.D.
External Advisory Committee, Gene Therapy Scientific Advisory Board
Dr. Clodagh O’Shea
Ph.D.
Gene Therapy Acceleration Committee
Dr. Jeffrey Rothstein
M.D., Ph.D.
External Advisory Committee
Dr. Brigitte Widemann
M.D.
External Advisory Committee
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Dr. June Lee
M.D.
External Advisory Committee
Bruce Korf
M.D., Ph.D.
External Advisory Committee
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Gilmore O’Neill
M.B., M.M.Sc.
Gene Therapy Scientific Advisor
Dr. Scott Plotkin
M.D., Ph.D.
Gene Therapy Acceleration Committee
Dr. Annette Bakker
Ph.D
External Advisory Committee, Gene Therapy Scientific Advisory Board
Dr. Dominic Esposito
Ph.D.
Scientific Advisory Board Committee
Angela Hirbe (FCS scholar)
M.D., Ph.D.
External Advisory Committee
Dr. Nicole Paulk
Ph.D.
Gene Therapy Scientific Advisory Board
Marcus Ratley
External Advisory Committee
Sally Gottesman
External Advisory Committee
Dr. Marco Giovannini
M.D., Ph.D.
External Advisory Committee
YooRi Kim
M.S.
Gene Therapy Scientific Advisory Board
Marjorie Tiven
MS
External Advisory Committee
Dr. Larry Blankstein
Ph.D.
External Advisory Committee, Gene Therapy Acceleration Committee
Bai Renyan
Dr. Renyuan Bai
M.B.B.S., Ph.D.
Gene Therapy Acceleration Committee and Gene Therapy Scientific Advisory Board

Staff

First Last Name,
M.D., Ph.D., Chair
Title

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