Meet the Global Team Working to Understand and Advance Treatments for NF1

The executive team that determines strategic priorities and directs our work.

The experts across neurology, dermatology, oncology, biotech, higher ed, engineering, and gene therapy who advise our work.

The team that brings our mission to life.

Executive Leadership

First Last Name,
M.D., Ph.D., Chair
Title

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Dr. Verena Staedtke

Advisors

Federico Mingozzi
Ph.D.
Gene Therapy Acceleration Committee
Dr. Lu Le
Lu Le
M.D., Ph.D.
External Advisory Committee, Gene Therapy Scientific Advisory Board
Clodagh O’Shea
Ph.D.
Gene Therapy Acceleration Committee
Jeffrey Rothstein
M.D., Ph.D.
External Advisory Committee
Brigitte Widemann
M.D.
External Advisory Committee
June Lee
June Lee
M.D.
External Advisory Committee
Bruce Korf
M.D., Ph.D.
External Advisory Committee
Gilmore O’Neill
Gilmore O’Neill
M.B., M.M.Sc.
Gene Therapy Scientific Advisor
Scott Plotkin
M.D., Ph.D.
Gene Therapy Acceleration Committee
Annette Bakker
Ph.D
External Advisory Committee, Gene Therapy Scientific Advisory Board
Dominic Esposito
Ph.D.
Scientific Advisory Board Committee
Angela Hirbe (FCS scholar)
M.D., Ph.D.
External Advisory Committee
Nicole Paulk
Ph.D.
Gene Therapy Scientific Advisory Board
Marcus Ratley
External Advisory Committee
Sally Gottesman
External Advisory Committee
Marco Giovannini
M.D., Ph.D.
External Advisory Committee
YooRi Kim
M.S.
Gene Therapy Scientific Advisory Board
Marjorie Tiven
MS
External Advisory Committee
Larry Blankstein
Ph.D.
External Advisory Committee, Gene Therapy Acceleration Committee
Bai Renyan
Renyuan Bai
M.B.B.S., Ph.D.
Gene Therapy Acceleration Committee and Gene Therapy Scientific Advisory Board

Staff

First Last Name,
M.D., Ph.D., Chair
Title

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